Dosage Thresholds and Influence of Transgene Cassette in Adeno-Associated Virus–Related Toxicity

Hanen Khabou; Chloé Cordeau; Laure Pacot; Sylvain Fisson; Deniz Dalkara

doi:10.1089/hum.2018.144

journal article Nov 01, 2018

Dosage Thresholds and Influence of Transgene Cassette in Adeno-Associated Virus–Related Toxicity

Hanen Khabou Chloé Cordeau Laure Pacot Sylvain Fisson

Deniz Dalkara

Human Gene Therapy Vol. 29 No. 11 pp. 1235-1241 · SAGE Publications

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Details

Published: Nov 01, 2018
Vol/Issue: 29(11)
Pages: 1235-1241
License: View

Authors

H

Hanen Khabou

Sorbonne Universités, UPMC Univ Paris 06, INSERM, CNRS, Institut de la Vision, Paris, France; and Inserm UMR_S951, Univ Evry, Université Paris-Saclay, EPHE, Evry, France.

C

Chloé Cordeau

Sorbonne Universités, UPMC Univ Paris 06, INSERM, CNRS, Institut de la Vision, Paris, France; and Inserm UMR_S951, Univ Evry, Université Paris-Saclay, EPHE, Evry, France.

L

Laure Pacot

Sorbonne Universités, UPMC Univ Paris 06, INSERM, CNRS, Institut de la Vision, Paris, France; and Inserm UMR_S951, Univ Evry, Université Paris-Saclay, EPHE, Evry, France.

S

Sylvain Fisson

Généthon, Inserm UMR_S951, Univ Evry, Université Paris-Saclay, EPHE, Evry, France.

D

Deniz Dalkara

Sorbonne Universités, UPMC Univ Paris 06, INSERM, CNRS, Institut de la Vision, Paris, France; and Inserm UMR_S951, Univ Evry, Université Paris-Saclay, EPHE, Evry, France.

Cite This Article

Hanen Khabou, Chloé Cordeau, Laure Pacot, et al. (2018). Dosage Thresholds and Influence of Transgene Cassette in Adeno-Associated Virus–Related Toxicity. Human Gene Therapy, 29(11), 1235-1241. https://doi.org/10.1089/hum.2018.144

Dosage Thresholds and Influence of Transgene Cassette in Adeno-Associated Virus–Related Toxicity

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